Tucson, AZ, and Downingtown, PA — December 4, 2017 — Critical Path Institute's (C-Path) Data Collaboration Center (DCC) and the Friedreich's Ataxia Research Alliance (FARA) have announced that they will work together to develop an aggregated database of clinical data for Friedreich's ataxia (FA). Use of this database will promote collaborative research to support the understanding of natural history, potential biomarkers, and potential clinical endpoints for patients with FA, which will help researchers develop more efficient clinical trial protocols to test new therapies more quickly and effectively.
"FA is a rare disease which is progressive, affects multiple organ systems, and is fatal. Treating the disease is an urgent unmet need. FA research has reached a critical juncture, where several therapies have undergone or are in clinical trials, and additional new therapies are expected to start clinical development in the next few years. The purpose of this project is to leverage and share as much information as possible, to more fully understand progression of disease, how that progression can be captured in measurable endpoints, and the effect of placebo treatment. We want to ensure that we are using all the information available to design the most efficient and robust clinical trials, giving potential therapies the best chance of success," explained Jennifer Farmer, FARA's Executive Director.
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