Funded Grants

FARA-Funded Research Grants

  • Reset

General Research Grant | Gene & Stem Cell Therapy

Grant Awarded | Dec 2022

Evaluation of ARMMs-mediated delivery of Cas9 protein complexed with gRNAs as a non-viral disease-modifying strategy for Friedreich’s Ataxia

Joseph Nabhan, PhD
Vesigen Therapeutics, Cambridge (MA)

Postdoctoral Fellowship | Mechanism or Pathway of Disease

Grant Awarded | Oct 2022

Illuminating how SynGRs liberate gene expression from heterochromatin

Sarah Robinson-Thiewes, PhD
St. Jude Children's Research Hospital

Postdoctoral Fellowship | Gene & Stem Cell Therapy

Grant Awarded | Oct 2022

Engineering adeno-associated viral vectors to evade immune responses

Changfan Lin, PhD
California Institute of Technology

Award for Innovative Mindset (AIM) | Improving Clinical Outcomes

Grant Awarded | Sep 2022

Functional electrical stimulation (FES) cycling training to improve motor and cardiac functions in patients with Friedreich’s Ataxia: a feasibility and efficacy study

Manuela Corti, PhD & Tanja Taivassalo, PhD
University of Florida

Postdoctoral Research Award | Mechanism or Pathway of Disease

Grant Awarded | Sep 2022

Calcium communication among intracellular compartments in FA patient-derived cells

Anna Stepanova, PhD
Weill Cornell Medical College

Kyle Bryant Translational Research Award | Outcome Measures & Biomarkers

Grant Awarded | Aug 2022

Detection and enhancement of tissue NAD+ levels in Friedreich’s Ataxia

Joseph Baur, PhD & Shana McCormack, MD
University of Pennsylvania and Children's Hospital of Philadelphia

Award for Innovative Mindset (AIM) | Outcome Measures & Biomarkers

Grant Awarded | Jun 2022

A New Ultrasensitive Single-Molecule Assay for Frataxin Measurement

Ankur Jain, PhD & Ricardo Mouro Pinto, PhD
Whitehead Institute for Biomedical Research, Harvard Medical School and Massachusetts General Hospital

General Research Grant | Mechanism or Pathway of Disease

Grant Awarded | Jun 2022

Rescue of Friedreich’s Ataxia cells by DNA methylation editing of the FXN gene

Shawn Liu, PhD & Joriene de Nooij, PhD
Columbia University

General Research Grant | Cell & Animal Models

Grant Awarded | May 2022

Investigating Proprioceptor Development and Function in Friedreich’s Ataxia

Mirella Dottori, PhD
University of Wollongong, Australia

General Research Grant | Outcome Measures & Biomarkers

Grant Awarded | Apr 2022

Diagnostic and Mechanistic Validation of a Metabolic Biomarker Panel to Guide Therapeutic Interventions in Friedreich’s Ataxia

Mark Payne, MD & Thomas O'Connell, PhD
Indiana University School of Medicine

General Research Grant | Mechanism or Pathway of Disease

Grant Awarded | Apr 2022

Novel Mitochondrial Targets for Friedreich’s Ataxia

Xinnan Wang, MD, PhD
Stanford University

General Research Grant | Outcome Measures & Biomarkers

Grant Awarded | Mar 2022

LEOPARD-FA: Longitudinal Endpoint Optimization to Provide an Assessment of Relevant Drugs in Friedreich’s Ataxia

Chad Heatwole, MD
University of Rochester Medical Center, NY