News & Blog

Press Release: Cellares and Papillon Therapeutics Partner to Automate Manufacturing of PPL-001 for Patients With Friedreich’s Ataxia

Community Statement: Update from Biogen

Meet the 2026 FARA Fellows

July 2026 – Advocacy Newsletter

Webinar Recording: PTC Therapeutics June 2026

Press Release: Larimar Therapeutics Reports Positive Open Label Data and Submission of First Module of Rolling BLA for Accelerated Approval of Nomlabofusp for Friedreich’s Ataxia

Webinar Recording: Lexeo Therapeutics May 2026

Press Release & Community Statement: Lexeo Therapeutics Announces Publication in JAMA Cardiology of Phase I/II Data for LX2006 in Friedreich Ataxia

Press Release: Update from Lexeo Therapeutics

May/June 2026 – Advocacy Newsletter

Webinar Recording: Solid Biosciences May 2026

Community Letter: Update from PTC Therapeutics