FARA, LEXEO Therapeutics, and Weill-Cornell Medical College hosted an informational webinar on Gene Therapy for the Heart in FA on June 27th. The presenters were Dr. Jay Barth, Chief Medical Officer, LEXEO Therapeutics and Dr. Ronald Crystal, Weill-Cornell Medical College; and the session was moderated by FARA.

This webinar provided information on an investigational gene therapy for the treatment of the cardiac manifestations of FA, including details on two clinical trials.

Summary Slides and FAQs from the Cornell/ LEXEO community webinar can be accessed here:
  1. Slides
  2. FAQs
  3. Unanswered audience questions

To learn more about gene therapy please visit: FARA’s Roadmap to Gene Therapy Readiness

Anyone considering participating in a clinical trial should discuss the matter with his or her physician. FARA does not endorse or recommend any particular studies.