News & Blog

2025 FA Swing for a Cure Tournament Recap

Meet the Community: Braxton Terrebonne

Lexeo Therapeutics Reports Second Quarter 2025 Financial Results and Operational Highlights

Meet the Community: Erin Solomon

Press Release & Community Statement: PTC Therapeutics Receives Complete Response Letter for Vatiquinone NDA

Meet the Community: Armin Mansory

August 2025 – Advocacy Newsletter

Meet the Community: Carla Poletti

Take Action to Raise Awareness for FA—Submit a Proclamation Request!

Job Posting: Research Portfolio Manager

FA Community Conversations FA Drug Development Pipeline Webinar: Recording Available on YouTube

Design Therapeutics Highlights Progress Across Lead GeneTAC® Programs and Reports Second Quarter 2025 Financial Results