News & Blog

Tunable genetic circuits to enable precision genetic medicines for Friedreich’s Ataxia

CBM-01, A Novel Inhibitor of Lipid Peroxidation for Targeting Iron-mediated Pathology in FA Cardiomyopathy  

Investigating Synthetic Gene Regulator function in FRDA patient-derived Cardiomyocytes and neuronal cell types

Pre-clinical assessment of protein replacement therapy in the central nervous system of Friedreich’s ataxia mouse models

Discovery of frataxin substitute drug candidates for the treatment of Friedreich’s Ataxia

Trojan nanobodies to increase frataxin function