News & Blog

Webinar Recording: Larimar June 2025 Update

Press Release & Community Statement: PTC Therapeutics Receives Complete Response Letter for Vatiquinone NDA

August 2025 – Advocacy Newsletter

Take Action to Raise Awareness for FA—Submit a Proclamation Request!

Job Posting: Research Portfolio Manager

FA Community Conversations FA Drug Development Pipeline Webinar: Recording Available on YouTube

Design Therapeutics Highlights Progress Across Lead GeneTAC® Programs and Reports Second Quarter 2025 Financial Results

Meet the 2025 FARA Fellows

Press Release and Community Statement: Lexeo Therapeutics Announces FDA Breakthrough Therapy Designation for LX2006 in Friedreich Ataxia

June/July 2025 – Advocacy Newsletter

Press Release: Muscular Dystrophy Association and Friedreich’s Ataxia Research Alliance Announce New Collaborative Grant to Study Cardiac Fibrosis in Friedreich’s Ataxia

Press Release: Larimar Therapeutics Announces FDA Recommendations on Safety Database, and Other Details of Nomlabofusp BLA Submission for Friedreich’s Ataxia Program