Evaluating the cardioprotective effect of omaveloxolone on Friedreich ataxia heart disease
Deliverable in vitro transcribed mRNAs of Frataxin as a therapeutic approach for Friedreich ataxia
Deriving Functional MRI Equivalent Biomarkers in Friedreich Ataxia solely using Brain Structure Data
Characterization of FA iPSC-derived DRG organoid to decipher neurodevelopmental and neurodegenerative mechanisms
Skeletal Muscle Fatigue and Abnormal Ca2+ Signaling in Friedreich’s Ataxia
Investigating microglial phenotypes and functions in the pathogenesis of Friedreich’s ataxia
Multimodal peripheral nervous system imaging to quantify, monitor, and understand the neuropathy of Friedreich ataxia
Targeting Novel Mitochondrial Pathways for Friedreich’s Ataxia Therapy
Dysregulated microglial Ca2+ homeostasis as a pathogenic contributor and therapeutic target in Friedreich’s ataxia
Paired Prime Editors to treat Friedreich’s Ataxia
Treatment of Friedreich’s ataxia using novel ferroptosis inhibitors
Developing and delivering of novel gene editing technologies to contract GAA repeats in Friedreich’s ataxia