Award for Innovative Mindset (AIM) | Mechanism or Pathway of Disease
Funded Grants
FARA-Funded Research Grants
Award for Innovative Mindset (AIM) | Mechanism or Pathway of Disease
The N-terminus of frataxin and its role in FRDA
Award for Innovative Mindset (AIM) | Cell & Animal Models
Rational design of new CNS neuronal models for selective vulnerability in FRDA
General Research Grant | Cardiac Research
Molecular and cellular mechanisms of cardiac fibrosis in Friedreich ataxia
Postdoctoral Research Award | Outcome Measures & Biomarkers
Enhancing Friedreich Ataxia Research: Data Augmentation and Multimodal Fusion Focusing on the Spine-Brain Axis
Postdoctoral Fellowship | Mechanism or Pathway of Disease
Inhibition of the TLR4 receptor prevents neuro-inflammation and degeneration in frataxin-deficient sensory neurons
General Research Grant | Gene & Stem Cell Therapy
Characterization of ocular phenotype of the YG8-800 mouse model of FA and retinal-targeted treatment by AAV based CRISPR-Cas9 gene editing
Postdoctoral Research Award | Mechanism or Pathway of Disease
Unraveling Epigenetic Mechanisms and Therapeutic Strategies for FXN Silencing in Friedreich’s Ataxia
General Research Grant | Gene & Stem Cell Therapy
Rescuing frataxin expression by alternative splicing reprogramming with base editing
General Research Grant | Gene & Stem Cell Therapy
Application of RSwitch technology to improve Friedreich’s ataxia viral gene therapy safety and efficacy: control of FXN transgene expression through a small molecule regulation
Award for Innovative Mindset (AIM) | Gene & Stem Cell Therapy
Development of Epigenetic Editors for Frataxin Reactivation
General Research Grant | Outcome Measures & Biomarkers