The Scientific Advisory Board serves as advisors on FARA’s scientific research priorities, goals and programs as well as medical issues that arise from FA and treatment implementation.
Key Responsibilities:
- A commitment to FARA's mission; advancing treatments & improving clinical outcomes for individuals with FA.
- A commitment to helping FARA grow and nurture the FA research community.
- To promote collaboration in the FA research community.
- Reviewing grants and making funding recommendations
- Assessing gaps in research portfolio and making recommendations for new opportunites/research directions
Co-Chairs
Bronya Keats, PhD
Emeritus Professor of Genetics, LSU Health Sciences Center
FARA, Chief Research Officer
Giovanni Manfredi, MD, PhD
Professor of Neurology and Neuroscience
Weill Cornell Medical College
Advisors
Sanjay Bidichandani, PhD
Section Head of Genetics, University of Oklahoma College of Medicine
Department of Pediatrics
FARA, Board of Directors
Joy Cavagnaro, PhD
President
Access BIO
Joel Gottesfeld, PhD
Professor Emeritus
Department of Molecular Medicine
Scripps Research Institute
Sidney Hecht, PhD
Director, Biodesign Center for Bioenergetics
Arizona State University
David Lynch, MD, PhD
Professor of Neurology
Children's Hospital of Philadelphia / University of Pennsylvania
Jane Larkindale, DPhil
Vice President of Clinical Science
PepGen
James McArthur, PhD
President and CEO
PepGen
FARA, Board of Directors
Marek Napierala, PhD
Department of Neurology
UT Southwestern
Massimo Pandolfo, MD, FAAN, FEAN
Professor (Clinical)
Department of Neurology and Neurosurgery
McGill University
Mark Payne, MD
Professor of Pediatrics (Cardiology)
Indiana University School of Medicine
Hélène Puccio, PhD
Research Director Inserm
Institut NeuroMyoGene (INMG)
Bernard Ravina, PhD
Entrepreneur in Residence, Atlas Venture
James Rusche, PhD
Independent Consultant
Pharma and Biotech Product Development
FARA, Board of Directors
Kevin Whittlesey, PhD
Principal
Dark Horse Consulting Group
Robert Wilson, PhD
Professor of Pathology and Laboratory Medicine
University of Pennsylvania