The Scientific Advisory Board serves as advisors on FARA’s scientific research priorities, goals and programs as well as medical issues that arise from FA and treatment implementation.
Key Responsibilities:
A commitment to FARA's mission; advancing treatments & improving clinical outcomes for individuals with FA.
A commitment to helping FARA grow and nurture the FA research community.
To promote collaboration in the FA research community.
Reviewing grants and making funding recommendations
Assessing gaps in research portfolio and making recommendations for new opportunites/research directions
Co-Chairs
Dr. Bronya Keats Emeritus Professor of Genetics, LSU Health Sciences Center FARA, Chief Research Officer
Dr. Giovanni Manfredi Professor of Neurology and Neuroscience Weill Cornell Medical College
Advisors
Dr. Sanjay Bidichandani Section Head of Genetics, University of Oklahoma College of Medicine Department of Pediatrics FARA, Board of Directors
Dr. Joy Cavagnaro President Access BIO
Dr. Joel Gottesfeld Professor Emeritus Department of Molecular Medicine Scripps Research Institute
Dr. Sidney Hecht Director, Biodesign Center for Bioenergetics Arizona State University
Dr. Arnulf Koeppen Professor of Neurology and Pathology Albany Medical College
Dr. David Lynch Professor of Neurology Children's Hospital of Philadelphia / University of Pennsylvania
Jane Larkindale, D.Phil. Executive Director Duchenne Regulatory Sciences Consortium at Critical Path Institute (C-Path)
Dr. James McArthur Venture Partner RA Capital Management, LP FARA, Board of Directors
Dr. Marek Napierala Department of Biochemistry and Molecular Genetics University of Alabama
Massimo Pandolfo, MD, FAAN, FEAN Professor (Clinical) Department of Neurology and Neurosurgery McGill University
Dr. Mark Payne Professor of Pediatrics (Cardiology) Indiana University School of Medicine
Dr. Helene Puccio Department of Neurobiology and Genetics Institute of Genetics and Molecular and Cellular Biology
Dr. Bernard Ravina Chief Medical OfficerPraxis Medicines
Dr. James Rusche Independent Consultant Pharma and Biotech Product Development FARA, Board of Directors
Dr. Kevin Whittlesey Vice President, Translational Medicine 4D Molecular Therapeutics
Dr. Robert Wilson Associate Professor of Pathology and Laboratory Medicine University of Pennsylvania