Investigating Proprioceptor Development and Function in Friedreich’s Ataxia
Diagnostic and Mechanistic Validation of a Metabolic Biomarker Panel to Guide Therapeutic Interventions in Friedreich’s Ataxia
Novel Mitochondrial Targets for Friedreich’s Ataxia
LEOPARD-FA: Longitudinal Endpoint Optimization to Provide an Assessment of Relevant Drugs in Friedreich’s Ataxia
Understanding ketogenesis in FRDA: Pathophysiology, biomarkers and nutritional therapies
Investigating epigenetic silencing in Friedreich’s Ataxia
Therapeutic activity of a haematopoietic stem cell delivered tissue penetrating peptide in a Friedreich’s ataxia mouse model