Accept Cookies?
Provided by OpenGlobal E-commerce

Please wait while your page loads ...

FARAFARA Cure FA

New developments in pharmacotherapy for Friedreich ataxia

Current and emerging therapies for Friedrich's Ataxia (FA) focus on reversing the deleterious effects of such deficiency including mitochondrial augmentation and increasing frataxin levels, providing the possibility of treatment options for this physiologically complex, multisystem disorder. In this review article, the authors discuss the current and prior in vivo and in vitro research studies related to the treatment of FA, with a particular interest in future implications of each therapy. Since the discovery of FXN in 1996, multiple clinical trials have occurred or are currently occurring; at a rapid pace for a rare disease. These trials have been directed at the augmentation of mitochondrial function and/or alleviation of symptoms and are not regarded as potential cures in FA. Either a combination of therapies or a drug that replaces or increases the pathologically low levels of frataxin better represent potential cures in FA.

Read the entire article HERE

About the Author

Jane Larkindale

SHARE

FacebookTwitterLinkedInYoutube
Family D.jpg

 

Archived in
  Scientific News


 

 

Tagged in
FARA Scientific News


Site Map     Privacy Policy     Service Terms     Log-in     Contact     Charity Navigator